Rocket Pharmaceuticals Withdraws Gene Therapy Application for Rare Blood Disorder
Rocket Pharmaceuticals, a New Jersey-based biotech company, has voluntarily withdrawn its biologics license application (BLA) for mozafancogene autotemcel, a gene therapy intended to treat Fanconi anemia, a rare blood disorder. This decision, announced in an SEC filing on October 6, 2025, marks a significant shift in the company's strategic focus and pipeline priorities.